Design, synthesis, nuclear localization, and biological activity of a fluorescent duocarmycin analog, HxTfA

Author(s)
Konstantinos Kiakos, Bernhard Englinger, Stephanie K. Yanow, Debora Wernitznig, Michael A. Jakupec, Walter Berger, Bernhard K. Keppler, John A. Hartley, Moses Lee, Pravin C. Patil
Abstract

HxTfA 4 is a fluorescent analog of a potent cytotoxic and antimalarial agent, TfA 3, which is currently being investigated for the development of an antimalarial vaccine, PlasProtect®. HxTfA contains a p-anisylbenzimidazole or Hx moiety, which is endowed with a blue emission upon excitation at 318 nm; thus enabling it to be used as a surrogate for probing the cellular fate of TfA using confocal microscopy, and addressing the question of nuclear localization. HxTfA exhibits similar selectivity to TfA for A-tract sequences of DNA, alkylating adenine-N3, albeit at 10-fold higher concentrations. It also possesses in vitro cytotoxicity against A549 human lung carcinoma cells and Plasmodium falciparum. Confocal microscopy studies showed for the first time that HxTfA, and by inference TfA, entered A549 cells and localized in the nucleus to exert its biological activity. At biologically relevant concentrations, HxTfA elicits DNA damage response as evidenced by a marked increase in the levels of γH2AX observed by confocal microscopy and immunoblotting studies, and ultimately induces apoptosis.

Organisation(s)
Department of Inorganic Chemistry
External organisation(s)
Medizinische Universität Wien, University of Alberta, Hope College, University College London, University of Vienna
Journal
Bioorganic & Medicinal Chemistry Letters
Volume
28
Pages
1342-1347
No. of pages
6
ISSN
0960-894X
DOI
https://doi.org/10.1016/j.bmcl.2018.03.016
Publication date
05-2018
Peer reviewed
Yes
Austrian Fields of Science 2012
104015 Organic chemistry, 301305 Medical chemistry
Keywords
ASJC Scopus subject areas
Drug Discovery, Molecular Medicine, Molecular Biology, Biochemistry, Clinical Biochemistry, Pharmaceutical Science, Organic Chemistry
Sustainable Development Goals
SDG 3 - Good Health and Well-being
Portal url
https://ucrisportal.univie.ac.at/en/publications/3ec861da-3518-474e-9430-4a747cb74f09